Keyword Connections

f508del

Journals

2

1 BMC pulmonary medicine

2 cell stem cell

Research Groups

0

No Research Group Connected

Bibliographies

3

1 High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia.

2 Use of ivacaftor in late diagnosed cystic fibrosis monozygotic twins heterozygous for F508del and R117H-7T - a case report.

3 functional rescue of f508del-cftr using small molecule correctors